GENV 002
Alternative Names: GENV-002Latest Information Update: 30 May 2025
At a glance
- Originator GeneVentiv Therapeutics
- Developer Duke University; GeneVentiv Therapeutics
- Class Gene therapies
- Mechanism of Action Alpha-glucosidase replacements; Gene transference
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Preclinical Glycogen storage disease type II
Most Recent Events
- 08 Apr 2025 Preclinical trials in Glycogen storage disease type II in USA (Parenteral), prior to April 2025
- 08 Apr 2025 GeneVentiv Therapeutics seeks IND approval for Glycogen storage disease type II in USA
- 08 Apr 2025 GeneVentiv Therapeutics plans a phase III trial for Glycogen storage disease type II (Parenteral)