IMM 4800
Alternative Names: IMM-4800Latest Information Update: 31 May 2025
At a glance
- Originator IMMvention Therapeutix
- Class Antianaemics; Small molecules
- Mechanism of Action BACH1 protein inhibitors
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Preclinical Sickle cell anaemia
Most Recent Events
- 10 May 2025 Preclinical trials in Sickle cell anaemia in USA (PO) prior to May 2025 (IMMvention Therapeutix Pipeline, May 2025)
- 10 May 2025 IMMvention Therapeutix announces intention to submit the regulatory application to the US FDA for Sickle cell anaemia (IMMvention Therapeutix Pipeline, May 2025)
- 10 May 2025 IMMvention Therapeutix plans a phase II/III trial for Sickle cell anaemia (IMMvention Therapeutix Pipeline, May 2025)