Research programme: AAV based gene therapies - Avista Therapeutics
Latest Information Update: 30 May 2025
At a glance
- Originator Avista Therapeutics
- Class Gene therapies
- Mechanism of Action Gene transference
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Preclinical Retinal disorders
Most Recent Events
- 30 Apr 2025 Preclinical trials in Retinal disorders in USA (Parenteral)