Research programme: antianaemic therapeutics - Fulcrum Therapeutics
Latest Information Update: 30 May 2025
At a glance
- Originator Fulcrum Therapeutics
- Class Antianaemics; Small molecules
- Mechanism of Action Undefined mechanism
-
Orphan Drug Status
No
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Preclinical Anaemia; Fanconi's anaemia
Most Recent Events
- 02 May 2025 Preclinical trials in Anaemia in USA (unspecified route) prior to May 2025
- 02 May 2025 Preclinical trials in Fanconi's anaemia in USA (unspecified route) prior to May 2025
- 21 Apr 2025 Fulcrum Therapeutics intends to file an IND application for Diamond-Blackfan anemia in the fourth quarter of 2025