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MDL 103

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Drug Profile

MDL 103

Alternative Names: MDL-103

Latest Information Update: 21 May 2025

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At a glance

  • Originator Modalis Therapeutics
  • Class Gene therapies
  • Mechanism of Action DUX4L1 protein expression modulators
  • Orphan Drug Status

    Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.

    No
  • New Molecular Entity No
  • Available For Licensing Yes

Highest Development Phases

  • Research Facioscapulohumeral muscular dystrophy

Most Recent Events

  • 12 May 2025 Early research in Facioscapulohumeral muscular dystrophy in Japan (Parenteral) (Modalis Therapeutics pipeline, May 2025)
  • 31 Dec 2023 MDL 103 is available for licensing as of 31 Dec 2023. https://www.modalistx.com/en/ 3896451

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