SAIL 0804
Alternative Names: SAIL-0804Latest Information Update: 17 Jun 2025
At a glance
- Originator Sail Biomedicines
- Class Gene therapies; RNA
- Mechanism of Action T lymphocyte replacements
-
Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Preclinical Autoimmune disorders