Research programme: RNA editing therapeutics - Rznomics
Latest Information Update: 04 Jul 2025
At a glance
- Originator Rznomics
- Class RNA
- Mechanism of Action RNA interference
-
Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Research Sensorineural hearing loss