PM 577
Alternative Names: PM-577Latest Information Update: 04 Jul 2025
At a glance
- Originator Prime Medicine
- Class Gene therapies
- Mechanism of Action Gene expression modulators
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Preclinical Hepatolenticular degeneration