Research programme: RNA interference therapeutics - Biogen/City Therapeutics
Latest Information Update: 04 Jul 2025
At a glance
- Originator Biogen; City Therapeutics
- Class Small interfering RNA
- Mechanism of Action RNA interference
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Research Neurological disorders