Research programme: enzyme replacement therapies - Chiesi/Key2Brain
Alternative Names: aMann-K2B programLatest Information Update: 27 Jun 2025
At a glance
- Originator Key2Brain
- Class Enzymes; Recombinant proteins
- Mechanism of Action Enzyme replacements
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Preclinical Lysosomal storage diseases