Elpida 02
Alternative Names: ELP-02; Elpida-02Latest Information Update: 10 Mar 2026
At a glance
- Originator Elpida Therapeutics
- Class Gene therapies
- Mechanism of Action Gene transference
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Orphan Drug Status
No
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Preclinical Charcot-Marie-Tooth disease