Gene edited autologous induced pluripotent stem cell based therapy - Aspen Neuroscience
Alternative Names: 004; Autologous iPSC-derived therapy - Aspen NeuroscienceLatest Information Update: 04 Jul 2025
At a glance
- Originator Aspen Neuroscience
- Class Gene therapies; Induced pluripotent stem cell therapies
- Mechanism of Action Cell replacements
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Preclinical Neurological disorders
Most Recent Events
- 25 Jun 2025 Preclinical trials in Neurological disorders in USA (Parenteral), prior to June 2025 (Aspen Neuroscience pipeline, June 2025)