CTX 213
Alternative Names: CTX213; Deviceless beta cell replacement - CRISPR TherapeuticsLatest Information Update: 27 Jun 2025
At a glance
- Originator CRISPR Therapeutics
- Class Gene therapies; Stem cell therapies
- Mechanism of Action Pancreatic beta cell replacements
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
- Available For Licensing Yes
Highest Development Phases
- Research Type 1 diabetes mellitus