LIN 2003
Alternative Names: LIN-2003; Recombinant arylsulfatase A - Linno PharmaceuticalsLatest Information Update: 21 Aug 2025
At a glance
- Originator Linno Pharmaceuticals
- Class Arylsulfatases; Enzymes; Hydrolases; Recombinant proteins
- Mechanism of Action Arylsulfatase replacements
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Orphan Drug Status
Yes - Metachromatic leukodystrophy
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Preclinical Metachromatic leukodystrophy
Most Recent Events
- 21 Aug 2025 Linno Pharmaceuticals plans to initiate a phase I trial for Metachromatic leukodystrophy in the US in 2025 (Linno Pharmaceuticals pipeline, August 2025)
- 14 Jul 2025 Linno Pharmaceuticals plans a phase I clinical trial Metachromatic leukodystrophy in 2025 (Linno Pharmaceuticals pipeline, July 2025)
- 31 Dec 2023 Preclinical trials in Metachromatic leukodystrophy in China (Parenteral), prior to December 2023 (Linno Pharmaceuticals pipeline, July 2025)