ASP 2957
Alternative Names: ASP-2957; MyoAAV3.8 engineered capsid - myosin heavy chain kinase 7 - human myotubularin; MyoAAV3.8-MHCK7-hMTM1Latest Information Update: 16 Jul 2025
At a glance
- Originator Astellas Gene Therapies
- Class Gene therapies
- Mechanism of Action Gene transference; Myotubularin expression stimulants
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Preclinical Congenital structural myopathies
Most Recent Events
- 08 Jul 2025 Preclinical trials in Congenital structural myopathies in USA (IV)
- 08 Jul 2025 Astellas Gene Therapies plans a phase I/II trial for Congenital structural myopathies (In neonates, In infants) in USA (IV) (NCT07052929)