THN ASO 1
Alternative Names: THN-ASO-1Latest Information Update: 24 Sep 2025
At a glance
- Originator Theranexus
- Class Antisense oligonucleotides
- Mechanism of Action TFEB protein stimulants
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Orphan Drug Status
No
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Research CNS disorders