A 001 - Theravia
Alternative Names: A-001 - TheraviaLatest Information Update: 29 Nov 2025
At a glance
- Originator Theravia
- Class Skin disorder therapies
- Mechanism of Action Undefined mechanism
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Orphan Drug Status
No
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
- Available For Licensing Yes
Highest Development Phases
- Preclinical Epidermolysis bullosa
Most Recent Events
- 21 Jul 2025 A 001 - Theravia is available for licensing as of 21 Jul 2025. https://www.theravia.com/partnering
- 21 Jul 2025 Preclinical trials in Epidermolysis bullosa in France (unspecified route), before July 2025 (Theravia pipeline, July 2025)