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MYO7A targeting gene therapy - Rescue Hearing

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Drug Profile

MYO7A targeting gene therapy - Rescue Hearing

Alternative Names: MYO7A targeting gene therapy

Latest Information Update: 29 Nov 2025

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At a glance

  • Originator Rescue Hearing
  • Class Gene therapies; Vestibular disorder therapies
  • Mechanism of Action Gene transference; Myosin VIIa replacements
  • Orphan Drug Status

    Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.

    No
  • New Molecular Entity No

Highest Development Phases

  • Preclinical Ear disorders; Usher syndromes

Most Recent Events

  • 22 Jul 2025 Preclinical trials in Ear disorders in USA (Parenteral), before July 2025 (Rescue Hearing pipeline, July 2025)
  • 22 Jul 2025 Preclinical trials in Usher syndromes in USA (Parenteral), before July 2025 (Rescue Hearing pipeline, July 2025)

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