STRC targeting gene therapy - Rescue Hearing
Alternative Names: STRC targeting gene therapyLatest Information Update: 29 Nov 2025
At a glance
- Originator Rescue Hearing
- Class Gene therapies
- Mechanism of Action Gene transference; STRC protein expression stimulants
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Orphan Drug Status
No
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Preclinical Deafness
Most Recent Events
- 22 Jul 2025 Preclinical trials in Deafness in USA (Parenteral), (Rescue Hearing pipeline, July 2025)