LOXHD1 targeting gene therapy - Rescue Hearing
Alternative Names: LOXHD1 targeting gene therapyLatest Information Update: 29 Nov 2025
At a glance
- Originator Rescue Hearing
- Class Gene therapies
- Mechanism of Action Gene transference
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Orphan Drug Status
No
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Preclinical Hearing loss
Most Recent Events
- 16 Sep 2025 Preclinical trials in Hearing loss in USA (Parenteral), before September 2025 (Rescue Hearing pipeline, September 2025)