ART 009
Alternative Names: ART-009Latest Information Update: 01 Aug 2025
At a glance
- Originator AccurEdit Therapeutics
- Class Gene therapies
- Mechanism of Action Gene transference
-
Orphan Drug Status
No
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Research Metabolic disorders
Most Recent Events
- 31 Dec 2024 Early research in Metabolic disorders in China (Parenteral), prior to July 2025 (AccurEdit Therapeutics pipeline, July 2025)
- 31 Dec 2024 AccurEdit Therapeutics plans IND-enabling studies for Metabolic disorders (AccurEdit Therapeutics pipeline, July 2025)