SYNGAP antisense oligonucleotide therapy - Quiver Bioscience
Alternative Names: SYNGAP (ASO)Latest Information Update: 25 Aug 2025
At a glance
- Originator Quiver Bioscience
- Class Antisense oligonucleotides
- Mechanism of Action Gene silencing; SYNGAP1 protein expression modulators
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Orphan Drug Status
No
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
- Available For Licensing Yes
Highest Development Phases
- Research Neurodevelopmental disorders
Most Recent Events
- 03 Aug 2025 Early research in Neurodevelopmental disorders in USA (Parenteral) prior to July 2025 (Quiver Bioscience pipeline; July 2025)
- 30 Jul 2025 SYNGAP (ASO) - Quiver Bioscience is available for licensing as of 30 Jul 2025. https://www.quiverbioscience.com/#platform