Drug Profile

Research programme: CNS disorders therapeutics - Apertura Gene Therapy/Undisclosed Company

Latest Information Update: 03 Sep 2025

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At a glance

Orphan Drug Status

Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.

No
New Molecular Entity No

13 Aug 2025 Undisclosed company in-licenses TfR1 CapX capsid technology from Apertura Gene Therapy
13 Aug 2025 Early research in CNS disorders in USA (Parenteral)

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