EDIT 401
Alternative Names: EDIT-401Latest Information Update: 07 Oct 2025
At a glance
- Originator Editas Medicine
- Class Antihyperlipidaemics; Gene therapies
- Mechanism of Action Gene transference
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Orphan Drug Status
No
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Preclinical Hyperlipidaemia
Most Recent Events
- 02 Sep 2025 Preclinical trials in Hyperlipidaemia in USA (Parenteral)
- 02 Sep 2025 Pharmacodynamics data from a preclinical trial in Hyperlipidemia released by Editas Medicine
- 02 Sep 2025 Editas Medicine plans to submit an IND application or Clinical Trial Application (CTA) to regulatory authorities, for initiating clinical trials in mid 2026