ATXN2 gene targeting exosome therapeutic - Evox therapeutics
Latest Information Update: 24 Sep 2025
At a glance
- Originator Evox Therapeutics
- Class Exosome therapies; Gene therapies
- Mechanism of Action Ataxin 2 modulators
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Orphan Drug Status
No
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Preclinical Amyotrophic lateral sclerosis; Spinocerebellar ataxias