CONF targeting gene therapy - Rescue Hearing
Latest Information Update: 27 Dec 2025
At a glance
- Originator Rescue Hearing
- Class Gene therapies
- Mechanism of Action Gene transference
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Orphan Drug Status
No
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Preclinical Neurological disorders
Most Recent Events
- 16 Sep 2025 Preclinical trials in Neurological disorders in USA (Parenteral), before September 2025 (Rescue Hearing pipeline, September 2025)