ART 9
Alternative Names: ART-9Latest Information Update: 28 Nov 2025
At a glance
- Originator Arnatar Therapeutics
- Class Antisense oligonucleotides
- Mechanism of Action Gene silencing
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Orphan Drug Status
No
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Research CNS disorders
Most Recent Events
- 17 Sep 2025 Early research in CNS disorders in USA (Parenteral), prior to September 2025 (Arnatar Therapeutics pipeline, September 2025)