Haemophilia A allogenic cell therapy - Sernova
Alternative Names: Haemophilia A allograft cell therapyLatest Information Update: 02 Dec 2025
At a glance
- Originator Sernova Corp
- Class Antihaemorrhagics; Cell therapies; Gene therapies
- Mechanism of Action Cell replacements; Factor VIII expression modulators
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Orphan Drug Status
Yes - Haemophilia A
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Research Haemophilia A
Most Recent Events
- 19 Sep 2025 Early research in Haemophilia A in Canada (SC) prior to September 2025 (Sernova pipeline, September 2025)
- 27 Nov 2023 Haemophilia A allogenic cell therapy receives Rare Pediatric Disease Designation for haemophilia A in USA
- 27 Nov 2023 Haemophilia A allogenic cell therapy receives Orphan Drug status for Haemophilia A in USA