HLX 0553
Alternative Names: HLX-0553Latest Information Update: 28 Nov 2025
At a glance
- Originator Healx
- Class
- Mechanism of Action Undefined mechanism
-
Orphan Drug Status
No
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Preclinical Angelman syndrome
Most Recent Events
- 09 Oct 2025 Preclinical trials in Angelman syndrome in United Kingdom (unspecified route), prior to October 2025 (Healx pipeline, October 2025)