SG 006
Alternative Names: SG-006Latest Information Update: 26 Dec 2025
At a glance
- Originator SineuGene Therapeutics
- Class Antisense oligonucleotides
- Mechanism of Action Ataxin 3 expression modulators
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Orphan Drug Status
No
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Preclinical Machado-Joseph Disease
Most Recent Events
- 11 Oct 2025 Preclinical trials in Machado-Joseph Disease in China (Parenteral) (Prior to October 2025) (SineuGene Therapeutics pipeline, October 2025)
- 11 Oct 2025 Preclinical trials in Machado-Joseph Disease in USA (Parenteral) (Prior to October 2025) (SineuGene Therapeutics pipeline, October 2025)