ION 775
Alternative Names: ION-775Latest Information Update: 28 Nov 2025
At a glance
- Originator Ionis Pharmaceuticals
- Class Antihyperlipidaemics; Small interfering RNA
- Mechanism of Action Apolipoprotein C-III inhibitors; RNA interference
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Orphan Drug Status
No
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Phase I Hypertriglyceridaemia
Most Recent Events
- 15 Oct 2025 Ionis Pharmaceuticals plans a phase II trial for Hypertriglyceridaemia in 2026 (Parenteral, Injection)
- 07 Oct 2025 Phase-I clinical trials in Hypertriglyceridaemia (In volunteers) (Parenteral)
- 07 Oct 2025 Efficacy and adverse events data from phase-I trial in Hypertriglyceridaemia rleased by Ionis pharmaceuticals