RTX 117
Alternative Names: RTX-117Latest Information Update: 09 Jan 2026
At a glance
- Originator ReviR Therapeutics
- Class RNA; Small molecules
- Mechanism of Action Eukaryotic initiation factor 2b modulators; RNA modulators
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Orphan Drug Status
Yes - Charcot-Marie-Tooth disease
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Preclinical Charcot-Marie-Tooth disease