ALXN 2350
Alternative Names: ALXN-2350Latest Information Update: 31 Oct 2025
At a glance
- Originator Alexion AstraZeneca Rare Disease
- Class Cardiovascular therapies; Gene therapies
- Mechanism of Action BAG3 protein replacements; Gene transference
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Orphan Drug Status
No
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Preclinical Dilated cardiomyopathy
Most Recent Events
- 20 Oct 2025 Preclinical trials in Dilated cardiomyopathy in USA (Parenteral) prior to October 2025
- 20 Oct 2025 Alexion Pharmaceuticals plans a (phase I/II trial for Dilated-cardiomyopathy in USA (IV, Infusion) in December 2025 (NCT07218887)