Research programme: hepatocyte nuclear factor 4 alpha targeted therapeutics - Arnatar Therapeutics
Latest Information Update: 21 Jan 2026
At a glance
- Originator Arnatar Therapeutics
- Class Antifibrotics; Antisense oligonucleotides
- Mechanism of Action Gene silencing; HNF4A protein expression stimulants
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Orphan Drug Status
No
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Preclinical Hepatic fibrosis