KNA 145
Alternative Names: KNA-145Latest Information Update: 01 Dec 2025
At a glance
- Originator Kinea Bio
- Class Gene therapies
- Mechanism of Action Gene transference
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Orphan Drug Status
No
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Preclinical Muscular dystrophies
Most Recent Events
- 30 Oct 2025 Preclinical trials in Muscular dystrophies in USA (Parenteral) before October 2025 (Kinea Bio pipeline, October 2025)