Research programme: gene therapies - Inozyme Pharma
Latest Information Update: 28 Nov 2025
At a glance
- Originator Inozyme Pharma
- Class Gene therapies
- Mechanism of Action Gene transference
-
Orphan Drug Status
No
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Research Unspecified
Most Recent Events
- 28 Oct 2025 Early research in Unspecified in USA (Parenteral) (Inozyme Pharma pipeline, October 2025)