UGX 301
Alternative Names: UGX-301Latest Information Update: 28 Nov 2025
At a glance
- Originator UgeneX Therapeutics
- Class Eye disorder therapies; Gene therapies
- Mechanism of Action Gene transference
-
Orphan Drug Status
No
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Research Dry macular degeneration
Most Recent Events
- 28 Oct 2025 Early research in Dry macular degeneration in China (Parenteral) (UgeneX Therapeutics pipeline, October 2025)