ESP 2001
Alternative Names: ESP-2001Latest Information Update: 26 Nov 2025
At a glance
- Originator Esperion Therapeutics
- Class Hepatoprotectants; Small molecules
- Mechanism of Action ATP citrate (pro S) lyase inhibitors
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Orphan Drug Status
No
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Preclinical Primary sclerosing cholangitis
Most Recent Events
- 07 Nov 2025 Esperion Therapeutics plans for Investigational new drug application (IND) in primary sclerosing cholangitis
- 06 Nov 2025 ESP 2001 licensed to Esperion Therapeutics worldwide for the treatment of Primary sclerosing cholangitis
- 06 Nov 2025 Esperion Therapeutics plans to apply for Fast track designation to the US FDA