BT 101 - BOOST Pharma
Alternative Names: BT-101 - BOOST PharmaLatest Information Update: 10 Jan 2026
At a glance
- Originator BOOST Pharma
- Class Mesenchymal stem cell therapies
- Mechanism of Action Cell replacements
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Orphan Drug Status
Yes - Osteogenesis imperfecta
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Phase I/II Osteogenesis imperfecta
Most Recent Events
- 11 Nov 2025 Phase-I/II clinical trials in Osteogenesis imperfecta (In infants, In neonates) in Sweden (IV) (NCT03706482)
- 31 Oct 2025 Efficacy data from a phase I/II BOOSTB4 trial in osteogenesis imperfecta released by BOOST Pharma
- 05 Nov 2024 BOOST Pharma plans to file an IND application with the US FDA in USA for osteogenesis imperfecta