ARO SNCA
Alternative Names: ARO-SNCALatest Information Update: 22 Jan 2026
At a glance
- Originator Arrowhead Pharmaceuticals
- Developer Arrowhead Pharmaceuticals; Novartis
- Class Antiparkinsonians; Small interfering RNA
- Mechanism of Action Alpha-synuclein expression inhibitors; RNA interference
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Orphan Drug Status
No
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Preclinical Parkinson's disease