DT 818
Alternative Names: DT-818Latest Information Update: 12 Nov 2025
At a glance
- Originator Design Therapeutics
- Class Small molecules
- Mechanism of Action Genetic transcription inhibitors
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Orphan Drug Status
No
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Preclinical Myotonic dystrophy