Ceruloplasmin - Kedrion Biopharma
Latest Information Update: 02 Dec 2025
At a glance
- Originator Kedrion Biopharma
- Class Alcohol oxidoreductases
- Mechanism of Action Enzyme replacements
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Orphan Drug Status
Yes - Familial apoceruloplasmin deficiency
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Preclinical Familial apoceruloplasmin deficiency
Most Recent Events
- 27 Nov 2025 Ceruloplasmin - Kedrion Biopharma receives Orphan Drug status for Familial apoceruloplasmin deficiency in European Union
- 07 Aug 2025 Ceruloplasmin - Kedrion Biopharma receives Orphan Drug status for Familial apoceruloplasmin deficiency in USA
- 30 Jan 2024 Preclinical trials in Familial apoceruloplasmin deficiency in USA (Intraperitoneal)