LRRK2 targeting small interfering RNA - Argo Biopharma
Latest Information Update: 01 Jan 2026
At a glance
- Originator Argo Biopharma
- Class Antiparkinsonians; Small interfering RNA
- Mechanism of Action LRRK2 protein expression modulators; RNA interference
-
Orphan Drug Status
No
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
- Available For Licensing Yes - Parkinson's disease
Highest Development Phases
- Research Parkinson's disease
Most Recent Events
- 10 Dec 2025 LRRK2 targeting small interfering RNA - Argo Biopharma is available for licensing as of 10 Dec 2025. https://www.argobiopharma.com/partnering/index.html (Argo Biopharma pipeline, December 2025)
- 10 Dec 2025 Early research in Parkinson's disease in China (Parenteral) (Argo Biopharma pipeline, December 2025)