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Sickle cell disease targeting RNA gene writers - Tessera Therapeutics

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Drug Profile

Sickle cell disease targeting RNA gene writers - Tessera Therapeutics

Alternative Names: In vivo gene rewriting therapies-Tessera Therapeutics

Latest Information Update: 15 Dec 2025

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At a glance

  • Originator Tessera Therapeutics
  • Class Antianaemics; Gene therapies; RNA
  • Mechanism of Action Beta-Globin expression modulators; Gene expression modulators
  • Orphan Drug Status

    Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.

    No
  • New Molecular Entity No

Highest Development Phases

  • Preclinical Sickle cell anaemia

Most Recent Events

  • 08 Dec 2025 Pharmacodynamics and pharmacokinetics data from a preclinical studies in Sickle cell anaemia released by Tessera therapeutics
  • 09 Dec 2024 Pharmacodynamics and pharmacokinetics data from a preclinical studies in Sickle cell anaemia released by Tessera therapeutics
  • 24 Oct 2024 Pharmacodynamics data from a preclinical studies in Sickle cell anaemia released by Tessera therapeutics

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