RN 3271
Alternative Names: RN-3271Latest Information Update: 17 Dec 2025
At a glance
- Originator Rona Therapeutics
- Class Cardiovascular therapies; RNA
- Mechanism of Action Prealbumin expression modulators; RNA interference
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Orphan Drug Status
No
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Preclinical Cardiomyopathies
Most Recent Events
- 17 Dec 2025 Preclinical trials in Cardiomyopathies in China (SC), before December 2025 (Rona Therapeutics pipeline, December 2025)