AB 1009
Alternative Names: AB-1009Latest Information Update: 30 Jan 2026
At a glance
- Originator Asklepios BioPharmaceutical
- Class Gene therapies
- Mechanism of Action Alpha-glucosidase replacements; Gene transference
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Orphan Drug Status
Yes - Glycogen storage disease type II
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Phase I/II Glycogen storage disease type II