VT 001 - Violet Therapeutics
Alternative Names: VT-001 - Violet TherapeuticsLatest Information Update: 05 Jan 2026
At a glance
- Originator Violet Therapeutics
- Class Neuroprotectants; Small molecules
- Mechanism of Action EphB3 receptor inhibitors
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Orphan Drug Status
No
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Preclinical Neurodegenerative disorders
Most Recent Events
- 23 Dec 2025 Violet Therapeutics plans to file an IND application in Japan for Neurodegenerative disorders in mid-2026 (Violet Therapeutics website, December 2025)
- 29 Jul 2025 Preclinical trials in Neurodegenerative disorders in USA (unspecified) prior to July 2025
- 29 Jul 2025 Pharmacodynamics and adverse events data from a preclinical studies in Neurodegenerative disorders presented at the Alzheimer's Association International Conference 2025 (AAIC-2025)