ALN 4285
Alternative Names: ALN-4285Latest Information Update: 26 Feb 2026
At a glance
- Originator Alnylam Pharmaceuticals
- Class Small interfering RNA
- Mechanism of Action RNA interference
-
Orphan Drug Status
No
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Phase I Unspecified
Most Recent Events
- 12 Feb 2026 Phase-I clinical trials in Unspecified (In volunteers) (SC) (Alnylam Pharmaceuticals pipeline, February 2026)
- 22 Dec 2025 Preclinical trials in Unspecified in USA (Parenteral) prior to December 2025
- 12 Dec 2025 Alnylam Pharmaceuticals plans a phase I trial for Healthy volunteers in United Kingdom (SC) in December 2025 (NCT07295717)