Research programme: RNA-targeting antisense oligonucleotide therapeutics - CAMP4 Therapeutics
Latest Information Update: 21 Jan 2026
At a glance
- Originator CAMP4 Therapeutics
- Developer GSK
- Class Antisense oligonucleotides; Urologics
- Mechanism of Action Gene silencing
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Orphan Drug Status
No
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Research Kidney disorders; Neurodegenerative disorders