APRTX 003
Alternative Names: APRTX-003Latest Information Update: 21 Jan 2026
At a glance
- Originator Aperture Therapeutics
- Class Antisense oligonucleotides; Neuroprotectants
- Mechanism of Action Gene silencing; Matrix metalloproteinase 9 modulators
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Orphan Drug Status
No
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
- Available For Licensing Yes
Highest Development Phases
- Preclinical Amyotrophic lateral sclerosis
Most Recent Events
- 19 Dec 2025 APRTX 003 is available for licensing as of 19 Dec 2025. https://www.aperturetx.com/
- 19 Dec 2025 Preclinical trials in Amyotrophic lateral sclerosis in USA (unspecified route) prior to December 2025 (Aperture therapeutics pipeline, December 2025)